admin

This first-in-human study of golodirsen showed its long-term safety and biologic activity in patients with Duchenne Muscular Dystrophy (DMD). The approved exon-skipping therapy is designed to enable the production of functional dystrophin proteins, as described in the peer-reviewed journal Nucleic Acid Therapeutics. Golodirsen was tested in ambulatory patients with exon 53 skip amenable DMD. They
0 Comments
Vanderbilt Kennedy Center (VKC) researchers, as part of the Centers for Disease Control and Prevention (CDC) Autism and Developmental Disabilities Monitoring (ADDM) network, report an increase in the number of children in Tennessee with autism spectrum disorder (ASD). The researchers published their findings in the CDC’s Morbidity and Mortality Weekly Report series on Dec. 2.
0 Comments
A Christmas Bucket List can help you capture the Christmas spirit and remember the reason for the season no matter what the age of your children. Picture what a stereotypical Old-Fashioned Christmas includes – tree decorating, cookie baking, gingerbread making, and Christmas caroling. Imagine if you had time what would you do this December –
0 Comments
Image: iStock IN THIS ARTICLE Stacking identical blocks, comparing two similar toys, putting together two sets of same books, and similar tasks reflect your toddler’s ability to match things. Knowing how one is matched to the other is some practical knowledge that they acquire by observing their surroundings. You can support their eagerness to learn
0 Comments
A bacterium common in the mouse gut microbiome can charge up the immune system to fight cancer cells in the colon, researchers from the University of Pittsburgh School of Medicine report today in the journal Immunity. The study showed that bacterium Helicobacter hepaticus boosted adaptive immune response and prompted selective activation of Helper T cells
0 Comments
Image: iStock IN THIS ARTICLE Social-emotional development of a toddler is a gradual and integrative process. It refers to the process of inculcating self-awareness, social skills, and self-control to maintain healthy relationships (1). Through this process, a toddler learns how to express, experience, understand, and manage emotions. And it enables them to build meaningful and
0 Comments
Many countries have implemented various nonpharmaceutical interventions (NPIs) such as social distancing mandates and lockdowns in response to the coronavirus disease 19 (COVID-19) pandemic. Although these measures reduced stress on the healthcare system in the absence of vaccines, they were associated with major socioeconomic costs. This led to a revival of the debate on whether
0 Comments
In pediatric and young adult patients with acute lymphoblastic leukemia (ALL) treated with tisagenlecleucel (Kymriah), DNA sequencing-based detection of residual disease between three and 12 months accurately identified all patients who would eventually relapse, while other methods were less predictive. Journal in Which the Study was Published: Blood Cancer Discovery, a journal of the American
0 Comments